News from NORD

January 12 Is Deadline for Rare Impact Awards Nominations


 

Nominate a colleague, patient, caregiver, or organization for a NORD Rare Impact Award online by January 12, 2018. These awards honor individuals or organizations for improving the lives of those affected by rare diseases. The awards are presented at NORD’s Rare Impact Awards event in Washington, DC in May. Over the years, those honored have included members of Congress, senior officials from FDA and NIH, clinicians, researchers, medical societies, patient organizations, and others whose work has had a beneficial impact on the community. More info .

Recommended Reading

Fenfluramine Reduces Convulsive Seizure Frequency in Dravet Syndrome
MDedge Neurology
Gene Therapy May Benefit Patients With Cerebral ALD
MDedge Neurology
Gene silencer reduces mutant huntingtin protein in early-stage Huntington’s patients
MDedge Neurology
Justin Gover
MDedge Neurology
Cardiosphere-derived cells may reverse Duchenne heart scarring
MDedge Neurology
Gene Replacement Improves Survival in Spinal Muscular Atrophy
MDedge Neurology
Cornelia de Lange Syndrome Foundation Call for Abstracts
MDedge Neurology
National Niemann-Pick Disease Foundation Seeks Executive Director
MDedge Neurology
National Tay-Sachs & Allied Diseases Association Grants Available
MDedge Neurology
Join 7,000 Miles Campaign to Support Programs for Rare Disease Patients
MDedge Neurology