Rare Diseases
News
FDA unveils 5-year plan for ALS and other neurodegenerative diseases
“We recognize the urgent need for new treatments that can both improve and extend the lives of people diagnosed with these diseases.”
News
Pandemic public health measures may have mitigated Kawasaki disease
Cohort study data suggest that actions to reduce the spread of COVID-19 also reduced exposure to Kawasaki disease triggers.
Opinion
Dodging potholes from cancer care to hospice transitions
The consequences of suboptimal hospice transitions can damage the mental health and well-being of patient and caregiver.
Conference Coverage
Dupilumab treats itch and clears lesions in prurigo nodularis patients
There are currently no Food and Drug Administration–approved systemic therapies for PN.
News
High early recurrence rates with Merkel cell carcinoma
Approximately 95% of all recurrences happened within 3 years of the initial diagnosis in the prospective cohort study.
News
New MIS-C guidance addresses diagnostic challenges, cardiac care
New updates in this third version of the American College of Rheumatology’s guidance include a recommendation for dual therapy with IVIg and...
News
Genes related to osteosarcoma survival identified
They predict survival and are also potential therapy targets.
Case Reports
Long-Term Successful Treatment of Indolent Systemic Mastocytosis With Omalizumab
Omalizumab may help prevent anaphylaxis and reduce disease burden associated with systemic mastocytosis, but further studies are needed to confirm...
Article
DART trial hits the target in angiosarcoma
Perspectives
COVID-19 vaccines and cancer patients: 4 things to know