Anemia
News
FDA grants drug orphan designation for PNH
The US Food and Drug Administration (FDA) has granted orphan drug designation to RA101495 for the treatment of paroxysmal nocturnal hemoglobinuria...
CME
Clinical Endpoints in PTCL: The Road Less Traveled
News
Thalassemia case provides insight into history of malaria
The earliest documented case of β-thalassemia in Sardinia suggests malaria was widespread on the island long before the Middle Ages, according to...
News
Models provide new understanding of sickle cell disease
Computer models have revealed new details of what happens inside a red blood cell affected by sickle cell disease (SCD), according to research...
News
CRISPR sheds light on dyskeratosis congenita
Gene editing has revealed how dyskeratosis congenita (DC) impairs the formation of blood cells, according to research published in Stem Cell...
News
Product granted fast track designation for aTTP
The US Food and Drug Administration (FDA) has granted fast track designation to caplacizumab, an anti-von Willebrand factor (vWF) nanobody being...
News
Predicting response to treatment in AML, MDS
Researchers say they have determined which patients will respond to treatment with SY-1425, a retinoic acid receptor alpha (RARα) agonist. The...
News
Tests reveal risk of passing on SCD, other diseases
Quest Diagnostics has announced the US launch of QHerit™, a genetic screening service that helps people of multiple ethnicities identify their...
From the Journals
Allele-matching in cord blood transplant yields better survival
Matching down to the allele level in umbilical cord blood transplantation between unrelated donors results in greater overall survival for those...
News
Predicting response to azacitidine in MDS
Research published in Cell Reports helps explain why some patients with myelodysplastic syndrome (MDS) do not respond to treatment with...
News
Mutations linked to Fanconi anemia
New research suggests that mutations in the RFWD3 gene cause Fanconi anemia (FA). Investigators detected mutations in the RFWD3 gene in a child...